Patients eligible for modulator drugs: Data from cystic fibrosis registry of Turkey

ÇOBANOĞLU, FATMA; ÖZÇELİK, HAYRİYE; Cakir, Erkan; ŞİŞMANLAR EYÜBOĞLU, TUĞBA; PEKCAN, SEVGİ; Cinel, Guzin; Yalcin, Ebru; Kiper, Nural; EMİRALİOĞLU ORDUKAYA, NAGEHAN; ŞEN, VELAT; ŞEN, HADİCE; Ercan, Omur; Cokugras, Haluk; KILINÇ SAKALLI, AYŞE; Al Shadfan, Lina; YAZAN, HAKAN; ALTINTAŞ, DERYA; KARAGÖZ IŞIK, DİLEK; DEMİR, ESEN; Ozturk, Gokcen; BİNGÖL, AYŞEN; BAŞARAN, ABDURRAHMAN; SAPAN, NİHAT; ÇEKİÇ, ŞÜKRÜ; DAMADOĞLU, EBRU; ASLAN, AYŞE; Gursoy, Tugba; Tugcu, Gokcen; Ozdemir, Ali; HARMANCI, KORAY; KILIÇ YILDIRIM, GONCA; KÖSE, MEHMET; Hangul, Melih; Tamay, Zeynep; Suleyman, Ayse; YÜKSEL, HASAN; YILMAZ, ÖZGE; Ozcan, Gizem; TOPAL, ERDEM; Can, Demet; KORKMAZ EKREN, PERVİN; Çaltepe, Gönül; KILIÇ, MEHMET; Ozdogan, Sebnem; DOĞRU ERSÖZ, DENİZ

doi:10.1002/ppul.24854

Patients eligible for modulator drugs: Data from cystic fibrosis registry of Turkey

ÇOBANOĞLU F. N., ÖZÇELİK H. U., Cakir E., ŞİŞMANLAR EYÜBOĞLU T., PEKCAN S., Cinel G., ...More

PEDIATRIC PULMONOLOGY, vol.55, no.9, pp.2302-2306, 2020 (SCI-Expanded, Scopus)

Publication Type: Article / Article
Volume: 55 Issue: 9
Publication Date: 2020
Doi Number: 10.1002/ppul.24854
Journal Name: PEDIATRIC PULMONOLOGY
Journal Indexes: Science Citation Index Expanded (SCI-EXPANDED), Scopus, CAB Abstracts, EMBASE, MEDLINE, Veterinary Science Database
Page Numbers: pp.2302-2306
Keywords: cystic fibrosis, modulator drugs, national registry, TEZACAFTOR-IVACAFTOR
Ondokuz Mayıs University Affiliated: Yes

Abstract

Background A better understanding of cystic fibrosis transmembrane conductance regulator biology has led to the development of modulator drugs such as ivacaftor, lumacaftor-ivacaftor, tezacaftor-ivacaftor, and elexacaftor-tezacaftor-ivacaftor. This cross-sectional study evaluated cystic fibrosis (CF) patients eligible for modulator drugs.